Gene replacement therapy restores RCBTB1 expression and cilium length in patient-derived retinal pigment epithelium

Gene replacement therapy restores RCBTB1 expression and cilium length in patient-derived retinal pigment epithelium.

Huang ZZhang DChen SC, Jennings L, Carvalho LS, Fletcher S, Chen FK, McLenachan S.

J Cell Mol Med. 2021 Nov;25(21):10020-10027. doi: 10.1111/jcmm.16911. Epub 2021 Oct 7.

PMID: 34617687

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